Prion Disease Treatment: Breakthroughs in Gene-Editing Therapy

April 7, 2025

Prion disease treatment has taken a significant leap forward, buoyed by groundbreaking research that offers hope for those affected by these rare and deadly conditions.Pioneering a novel approach, Sonia Vallabh and Eric Minikel are at the forefront of prion disease research, focusing on gene-editing therapy to combat disorders like fatal familial insomnia.
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